CarlsbadThe Food and Drug Administration approved a first-of-its-kind rare-disease drug.
It is the first treatment for Alexander disease, which had only supportive care.
In the trial, walking speed stayed stable on the drug versus a 33% decline for controls.
Ionis has not yet disclosed what price it will set for Zanvastro.
How each outlet framed it
- STAT
- emphasizes treatment stabilized walking speed (33% decline in control) and hints early treatment of children improves motor function
Sources: STAT